Congenital Hematological Disease Drug
Congenital hematological diseases affect the production or function of blood cells, clotting factors, or hemoglobin. Treatment varies depending on the specific disorder and may include supportive care, replacement therapies, targeted drugs, or advanced treatments such as gene therapy for eligible patients.
Common Congenital Hematological Diseases
Sickle cell disease
Beta thalassemia
Hemophilia A
Hemophilia B
Von Willebrand disease
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